Rare Diseases Weekly News - April 17th 2025
This Week in Rare Disease Breakthroughs 🧬 | Gene Therapies, Drug Approvals…
How a mid-size pharma in the prostate cancer space used insights to adapt its drug development program and marketing efforts.
The Challenge: Mapping prostate cancer stage and identifying key stakeholders…
How a pharma in the multiple myeloma space gained access to leading KOLs insights and used them in its asset development process.
The Challenge: Understanding how KOLs define the treatment evolution and the…
How can we address challenges in rare disease drug development?
It is estimated that rare diseases affect more than 400 million people…
Replication/ reproducibility crisis in preclinical studies. Is the end "in sight"?
Scientific development relies on knowledge/research credibility and validity.…
What a Linkedin poll revealed about the Gene Therapy challenges.
With over 2 million groups where professionals from various industries network,…
